At Sarepta, we are working with urgency to develop breakthrough therapies to treat genetic diseases.

Jacob and Hudson living with DMD

Our Products

Sarepta has four FDA-approved therapies. 

Our Pipeline

Our Pipeline

Sarepta is at the forefront of precision genetic medicine.

Clinical Trials

Sarepta Clinical Trials

Sarepta is committed to creating breakthrough treatments for people whose lives are being cut short and burdened by rare diseases. Fundamental to that mission are carefully designed and conducted clinical trials.

Patient Support

Treatment Access Programs

Our access programs include the SareptAssist Patient Support Program and Compassionate Use Policy and Managed Access Program (MAP).